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Results for “United Kingdom”
Sponsor: Purespring Therapeutics Limited
Immunoglobulin A (IgA) Nephropathy
United States, United Kingdom
Sponsor: AstraZeneca
Heart Failure With Preserved Ejection Fraction (HFpEF) · Heart Failure With Mildly Reduced Ejection Fraction (HFmrEF)
United States, Argentina, Australia, Austria, Brazil +27 more
- Real World Clinical Outcomes With Novel Modulator Therapy Combinations in People With CF (RECOVER)Active Not Recruiting
Sponsor: Royal College of Surgeons, Ireland
Cystic Fibrosis · Cystic Fibrosis Liver Disease · Cystic Fibrosis in Children · Adherence, Medication
Ireland, United Kingdom
Sponsor: Takeda
Immune Thrombocytopenic Purpura (ITP)
United States, Australia, Bulgaria, China, Croatia +10 more
- A Research Study on How Well Semaglutide Helps Children and Teenagers With Excess Body Weight Lose WeightActive Not Recruiting
Sponsor: Novo Nordisk A/S
Obesity
United States, Austria, Belgium, Denmark, Germany +5 more
- Long-term Extension of GTX-102 in Angelman SyndromeActive Not Recruiting
Sponsor: Ultragenyx Pharmaceutical Inc
Angelman Syndrome
United States, Australia, Canada, France, Germany +3 more
Sponsor: Inari Medical
Venous Thromboembolism · Deep Venous Thrombosis · Post-Thrombotic Syndrome
United States, Austria, Finland, Germany, Switzerland +1 more
- A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam (RO7034067) in Participants With Spinal Muscular AtrophyActive Not Recruiting
Sponsor: Hoffmann-La Roche
Spinal Muscular Atrophy (SMA)
United States, Australia, Belgium, Canada, Croatia +7 more
Sponsor: AbbVie
Non Small Cell Lung Cancer
United States, Argentina, Australia, Austria, Belgium +27 more
Sponsor: AbbVie
Acute Myeloid Leukemia
United States, Australia, France, Italy, South Korea +2 more
- A Safety and Tolerability Trial Evaluating CTX310 in Participants With Refractory DyslipidemiasRecruiting
Sponsor: CRISPR Therapeutics AG
Cardiovascular · Metabolic Disease · Dyslipidemias · Lipid Disorder
United States, Australia, New Zealand, United Kingdom
Sponsor: AstraZeneca
Healthy Participants · Obesity
United States, United Kingdom
Sponsor: Vividion Therapeutics, Inc.
Colorectal Adenocarcinoma
United States, Argentina, Belgium, Brazil, China +16 more
- Safety and Efficacy Trial of Epcoritamab Combinations in Subjects With B-cell Non-Hodgkin Lymphoma (B-NHL)Active Not Recruiting
Sponsor: Genmab
Diffuse Large B-Cell Lymphoma · Follicular Lymphoma
United States, Australia, Belgium, Czechia, Denmark +8 more
- Chemo Brain Prehab ProjectRecruiting
Sponsor: Dr. Chris Gaffney
Colorectal Cancer · Older Adults (60 - 85 Years Old) · Physically Inactive · Chemotherapy
United Kingdom
Sponsor: Stemline Therapeutics, Inc.
Breast Neoplasms · Brain Neoplasms · Neoplasms by Site · Neoplasms
United States, Belgium, France, Germany, Greece +5 more
Sponsor: CSL Behring
Secondary Immune Deficiency
United States, Belgium, Canada, Czechia, Denmark +6 more
Sponsor: EMD Serono Research & Development Institute, Inc.
Metastatic Colorectal Cancer
United States, Argentina, Australia, Austria, Belgium +11 more
Sponsor: Merck Sharp & Dohme LLC
Pulmonary Arterial Hypertension
United States, Argentina, Australia, Belgium, Brazil +22 more
Sponsor: Merck Sharp & Dohme LLC
Coronavirus Disease (COVID-19)
United States, Argentina, Brazil, Bulgaria, Colombia +19 more
- A Safety and Efficacy Study of GTX-102 in Subjects With Deletion- or Nondeletion-type Angelman Syndrome (AS)Active Not Recruiting
Sponsor: Ultragenyx Pharmaceutical Inc
Angelman Syndrome
United States, Argentina, Brazil, France, Israel +3 more
- Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)Completed
Sponsor: Travere Therapeutics, Inc.
Homocystinuria Due to CBS Deficiency
United States, Ireland, Qatar, United Kingdom
Sponsor: Wave Life Sciences USA, Inc.
Amyotrophic Lateral Sclerosis · Frontotemporal Dementia
Netherlands, United Kingdom
Sponsor: Vertex Pharmaceuticals Incorporated
Proteinuric Kidney Disease
United States, Belgium, Brazil, Canada, Colombia +8 more
Sponsor: University of Aberdeen
Takotsubo Cardiomyopathy · Myocardial Infarction
United Kingdom